Long-term stabilization after bone marrow transplantation in juvenile metachromatic leukodystrophy.
نویسندگان
چکیده
W e describe a 16-year-old boy with juvenile metachromatic leukodystrophy who was treated with bone marrow transplantation. Follow-up over 8 years showed no increase in symptoms, no progression of neurological signs, and no neuropsychological deterioration. We conclude that bone marrow transplantation may increase brain levels of arylsulfatase A enough to prevent deterioration in patients with juvenile metachromatic leukodystrophy. Arch Neurol. 1998;55:98-99
منابع مشابه
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ورودعنوان ژورنال:
- Archives of neurology
دوره 55 1 شماره
صفحات -
تاریخ انتشار 1998